• Age Limit

    • Selected Age Limit:
      1 to 75 Years

    • Gender

  • Apply
  • Clear

Trials in Diseases and Abnormalities at or Before Birth

708 Studies Found

A Study to Investigate the Pharmacokinetics, Safety, and Tolerability of Emicizumab in Healthy Chinese Volunteers

Location: China
Status: Recruiting
Phase: Phase 1
Results: N/A
Start Date: 20 Mar, 2018
Completion Date: 30 Oct, 2018
Healthy VolunteersHemophilia A

Extension at 10 Years of the: "Observational Study Evaluating Efficacy and Costs of Secondary Prophylaxis vs On-demand Therapy With Kogenate Bayer in Patients With Severe Haemophilia A."

Location: Italy
Status: Active, not recruiting
Results: N/A
Start Date: 14 Apr, 2016
Completion Date: 20 Mar, 2018
Hemophilia A

Efficacy and Safety of Rivipansel (GMI-1070) in the Treatment of Vaso-Occlusive Crisis in Hospitalized Subjects With Sickle Cell Disease

Location: Canada, United States
Status: Recruiting
Phase: Phase 3
Results: N/A
Start Date: 01 Jun, 2015
Completion Date: 01 Nov, 2018
AnemiaSickle Cell

Safety and Efficacy of BAY94-9027 in Previously Treated Male Children With Haemophilia A

Location: Argentina, Austria, Belgium, Bulgaria, Canada, Greece, Israel, Italy, Lithuania, Netherlands, New Zealand, Norway, Poland, Romania, Spain, United Kingdom, United States
Status: Active, not recruiting
Phase: Phase 3
Results: N/A
Start Date: 29 May, 2013
Completion Date: 17 Feb, 2020
Hemophilia A

Nonmyeloablative Haploidentical Peripheral Blood Mobilized Hematopoietic Precursor Cell Transplantation for Severe Congenital Anemias Including Sickle Cell Disease and Beta-Thalassemia

Location: United States
Status: Active, not recruiting
Phase: Phase 1/Phase 2
Results: N/A
Start Date: 09 Sep, 2009
Completion Date: 01 Aug, 2018
Peripheral Blood Stem Cell TransplantationAnemiaSickle CellGraft-Versus-Host DiseaseSirolimus (Rapamune )Alemtuzumab (Campath )

Clinical and Genetic Studies of VACTERL Association

Location: United States
Status: Completed
Results: N/A
Start Date: 29 Sep, 2008
Completion Date: 29 Jun, 2017
Congenital AbnormalitiesBirth DefectsCongenital Defects

Blood Sampling for Research Related to Sickle Cell Disease

Location: United States
Status: Enrolling by invitation
Results: N/A
Start Date: 09 Oct, 2007
Sickle Cell TraitSickle Cell DiseaseSickle Cell Anemia

Safety and Dose Escalation Study of an Adeno-Associated Viral Vector for Gene Transfer in Hemophilia A Subjects

Location: United States
Status: Recruiting
Phase: Phase 1/Phase 2
Results: N/A
Start Date: 01 Mar, 2018
Completion Date: 30 Jun, 2022
Hemophilia A

National Study of a Pharmacokinetic-Focused Educational Package for Patients With Severe Haemophilia A

Location: United Kingdom
Status: Completed
Results: N/A
Start Date: 01 Sep, 2015
Completion Date: 30 Nov, 2017
Hemophilia A

GCSF Adjunct Therapy for Biliary Atresia

Location: United States
Status: Enrolling by invitation
Phase: Early Phase 1
Results: N/A
Start Date: 15 Jan, 2018
Completion Date: 31 Jan, 2019
Biliary Atresia

Featured Doctors

Carlo Paribello
M.S.M., M.D
Brampton, Ontario, Canada
Loretta Rozario
Rheumatologists
Nelson, Fairfield, Australia
Lisa Schwartzman
Psychologist
Canada
Alicia Ordonez
Psychologist
Winnipeg, Manitoba, Canada
Ratna Merugumalla
Consultant in Emergency Medicine and Paediatric Em
Peterborough, Cambridgeshire, United Kingdom